Alnylam Pharmaceuticals, Inc.
Compositions and Methods for Treating Transthyretin (TTR) Mediated Amyloidosis

Abstract:

Disclosed herein are methods for treating hereditary transthyretin-mediated amyloidosis (hATTR amyloidosis) in a human patient in need thereof by administering an effective amount of a transthyretin (TTR)-inhibiting composition.