bluebird bio, Inc.
PCSK9 ENDONUCLEASE VARIANTS, COMPOSITIONS, AND METHODS OF USE
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Abstract:
The present disclosure provides improved genome editing compositions and methods for editing a PCSK9 gene. The disclosure further provides genome edited cells for the prevention, treatment, or amelioration of at least one symptom of hypercholesterolemia or a condition associated therewith.
Status:
Application
Type:
Utility
Filling date:
4 Oct 2018
Issue date:
3 Dec 2020