Intellia Therapeutics, Inc.
Compositions and Methods for Lactate Dehydrogenase (LDHA) Gene Editing

Last updated:

Abstract:

Compositions and methods for editing, e.g., introducing double-stranded breaks, within the LDHA gene are provided. Compositions and methods for treating subjects having hyperoxaluria are provided.

Status:
Application
Type:

Utility

Filling date:

25 Mar 2021

Issue date:

22 Jul 2021