Intellia Therapeutics, Inc.
METHODS FOR THE TREATMENT OF DISEASE WITH GENE EDITING SYSTEMS

Abstract:

Provided herein are methods of selectively treating a patient with a gene editing system on the basis of ascertaining the presence of a target sequence, at a target locus, that is fully complementary to a targeting domain of said gene editing system and/or on the basis of ascertaining the absence of a target sequence, at a locus other than the target locus, that is fully complementary to a targeting domain of said gene editing system.