Ionis Pharmaceuticals, Inc.
Modulation of SMN expression
Last updated:
Abstract:
Certain embodiments are directed to methods and compounds for inhibiting SMN-NAT, the natural antisense transcript of SMN. Such methods and compounds are useful for increasing expression of SMN in cells and animals.
Status:
Grant
Type:
Utility
Filling date:
11 Apr 2016
Issue date:
1 Dec 2020