Ionis Pharmaceuticals, Inc.
MODULATION OF TRANSTHYRETIN EXPRESSION

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Abstract:

Provided herein are methods, compounds, and compositions for reducing expression of transthyretin mRNA and protein in an animal. Such methods, compounds, and compositions are useful to treat, prevent, delay, or ameliorate transthyretin amyloidosis, or a symptom thereof.

Status:
Application
Type:

Utility

Filling date:

1 Jun 2020

Issue date:

1 Apr 2021