Ionis Pharmaceuticals, Inc.
Selective Reduction of Allelic Variants

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Abstract:

Disclosed herein are antisense compounds and methods for selectively reducing expression of an allelic variant of a huntingtin gene containing a single nucleotide polymorphism (SNP). Such methods, compounds, and composition are useful to treat, prevent, or ameliorate Huntington's Disease (HD).

Status:
Application
Type:

Utility

Filling date:

14 Jan 2020

Issue date:

3 Dec 2020