Sarepta Therapeutics, Inc.
COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY
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Abstract:
Improved compositions and methods for treating muscular dystrophy by administering antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping are described.
Status:
Application
Type:
Utility
Filling date:
7 Jun 2019
Issue date:
6 Feb 2020