Alexion Pharmaceuticals, Inc.
Methods of treating Mucopolysaccharidosis IIIB (MPSIIIB)
Last updated:
Abstract:
Methods for treating the central nervous system (CNS) in a human patient with mucopolysaccharidosis (MPS) MB who has an intact blood brain barrier, comprising intravenous administration of recombinant NaGlu.
Status:
Grant
Type:
Utility
Filling date:
29 Sep 2015
Issue date:
17 Sep 2019