Acer Therapeutics Inc.
Palatable compositions including sodium phenylbutyrate and uses thereof
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Abstract:
The present invention features palatable pharmaceutical compositions including sodium phenylbutyrate and methods for the treatment of inborn errors of metabolism (e.g., Maple Syrup Urine Disease or Urea Cycle Disorders), neurodegenerative disorders such as Parkinson's disease, spinal muscular atrophy, dystonia, or inclusion-body myositis with such compositions.
Status:
Grant
Type:
Utility
Filling date:
9 Mar 2021
Issue date:
26 Oct 2021