Applied Genetic Technologies Corporation
TRIPLE FUNCTION ADENO-ASSOCIATED VIRUS (AAV)VECTORS FOR THE TREATMENT OF C9ORF72 ASSOCIATED DISEASES

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Abstract:

The present disclosure provides isolated promoters, transgene expression cassettes, vectors, kits, and methods for treatment of C9ORF72 associated diseases, including ALS and FTD.

Status:
Application
Type:

Utility

Filling date:

22 Oct 2020

Issue date:

20 May 2021