Beam Therapeutics Inc.
COMPOSITIONS AND METHODS FOR TREATING GLYCOGEN STORAGE DISEASE TYPE 1A
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Abstract:
The invention provides compositions comprising novel adenosine base editors (e.g., ABE8) that have increased efficiency and methods of using base editors comprising adenosine deaminase variants for altering mutations associated with Glycogen Storage Disease Type 1a (GSD1a).
Status:
Application
Type:
Utility
Filling date:
13 Feb 2020
Issue date:
28 Apr 2022