Ionis Pharmaceuticals, Inc.
MODULATION OF GYS1 EXPRESSION

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Abstract:

Provided herein are methods, compounds, and compositions for reducing expression of GYS1 in an individual. Such methods, compounds, and compositions are useful to treat, prevent, delay, or ameliorate a glycogen storage disease or disorder in an individual in need.

Status:
Application
Type:

Utility

Filling date:

23 Dec 2021

Issue date:

14 Apr 2022