Sangamo Therapeutics, Inc.
METHODS AND COMPOSITIONS FOR THE TREATMENT OF FABRY DISEASE
Last updated:
Abstract:
Nucleases and methods of using these nucleases for inserting a sequence encoding a therapeutic .alpha.-Gal A protein such as an enzyme into a cell, thereby providing proteins or cell therapeutics for treatment and/or prevention of Fabry disease.
Status:
Application
Type:
Utility
Filling date:
10 Jan 2022
Issue date:
1 Sep 2022