Sangamo Therapeutics, Inc.
METHODS AND COMPOSITIONS FOR TREATING HUNTINGTON'S DISEASE
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Abstract:
Disclosed herein are compositions comprising non-naturally occurring zinc finger domains, fusion proteins comprising these zinc finger domains, polynucleotides encoding these proteins, cells expressing these proteins and pharmaceutical compositions comprising these proteins or polynucleotides as well as methods of modifying an Htt gene using these compositions for treating or preventing Huntington's Disease.
Status:
Application
Type:
Utility
Filling date:
16 Nov 2020
Issue date:
4 Mar 2021