Sangamo Therapeutics, Inc.
METHODS AND COMPOSITIONS FOR THE TREATMENT OF FABRY DISEASE
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Abstract:
The present disclosure provides expression constructs comprising a GLA transgene encoding the at least one .alpha.-Gal A protein for use in expressing .alpha.-Gal A proteins and preventing, inhibiting or treating Fabry disease or one or more symptoms associated with Fabry disease.
Status:
Application
Type:
Utility
Filling date:
3 Jan 2020
Issue date:
30 Jul 2020