Sangamo Therapeutics, Inc.
METHODS AND COMPOSITIONS FOR THE TREATMENT OF LYSOSOMAL STORAGE DISEASES
Last updated:
Abstract:
Nucleases and methods of using these nucleases for inserting a sequence encoding a therapeutic protein such as an enzyme into a cell, thereby providing proteins or cell therapeutics for treatment and/or prevention of a lysosomal storage disease.
Status:
Application
Type:
Utility
Filling date:
2 Apr 2019
Issue date:
25 Jul 2019