Sarepta Therapeutics, Inc.
COMPOSITIONS FOR TREATING MUSCULAR DYSTROPHY

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Abstract:

Improved compositions and methods for treating muscular dystrophy by administering antisense molecules capable of binding to a selected target site in the human dystrophin gene to induce exon skipping are described.

Status:
Application
Type:

Utility

Filling date:

21 Oct 2021

Issue date:

3 Feb 2022