Sarepta Therapeutics, Inc.
ANTISENSE-INDUCED EXON EXCLUSION IN MYOSTATIN
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Abstract:
The present disclosure relates to antisense oligomers and related compositions and methods for decreasing the expression of functional human myostatin and methods for treating muscular dystrophy and related disorders and more specifically relates to inducing exclusion of myostatin exon 2 and thereby reducing levels of myostatin protein.
Status:
Application
Type:
Utility
Filling date:
15 Apr 2021
Issue date:
24 Mar 2022