Sarepta Therapeutics, Inc.
EXON SKIPPING OLIGOMERS AND OLIGOMER CONJUGATES FOR MUSCULAR DYSTROPHY
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Abstract:
Antisense oligomers and antisense oligomer conjugates complementary to a selected target site in the human dystrophin gene to induce exon 53 skipping are described.
Status:
Application
Type:
Utility
Filling date:
13 Jun 2019
Issue date:
22 Jul 2021