Stoke Therapeutics, Inc.
METHODS AND COMPOSITIONS FOR TREATMENT OF CHOLESTERYL ESTER STORAGE DISEASE

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Abstract:

Provided herein are methods and compositions for treating a subject in need thereof, such as a subject with deficient LAL protein expression or a subject having Cholesteryl Ester Storage Disease.

Status:
Application
Type:

Utility

Filling date:

3 May 2019

Issue date:

2 Dec 2021