Stoke Therapeutics, Inc.
METHODS AND COMPOSITIONS FOR TREATMENT OF CHOLESTERYL ESTER STORAGE DISEASE
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Abstract:
Provided herein are methods and compositions for treating a subject in need thereof, such as a subject with deficient LAL protein expression or a subject having Cholesteryl Ester Storage Disease.
Status:
Application
Type:
Utility
Filling date:
3 May 2019
Issue date:
2 Dec 2021