Telesis Bio, Inc.
Codon-optimized CFTR MRNA
Last updated:
Abstract:
The present invention provides, among other things, improved methods and pharmaceutical compositions for treating cystic fibrosis based on codon optimized mRNA encoding a Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) protein.
Status:
Grant
Type:
Utility
Filling date:
27 Feb 2018
Issue date:
22 Feb 2022