Telesis Bio, Inc.
Novel Codon-Optimized CFTR MRNA

Last updated:

Abstract:

The present invention provides, among other things, improved methods and pharmaceutical compositions for treating cystic fibrosis based on codon optimized mRNA encoding a Cystic Fibrosis Transmembrane Conductance Regulator (CFTR) protein.

Status:
Application
Type:

Utility

Filling date:

6 Jan 2022

Issue date:

23 Jun 2022