Voyager Therapeutics, Inc.
Compositions and methods of treating amyotrophic lateral sclerosis (ALS)

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Abstract:

The present invention relates to small interfering RNA (siRNA) molecules against the SOD1 gene, adeno-associated viral (AAV) vectors encoding siRNA molecules and methods for treating amyotrophic lateral sclerosis (ALS) using the siRNA molecules and AAV vectors.

Status:
Grant
Type:

Utility

Filling date:

28 Jan 2020

Issue date:

16 Feb 2021