Alnylam Pharmaceuticals, Inc.
POLYNUCLEOTIDE AGENTS TARGETING HYDROXYACID OXIDASE (GLYCOLATE OXIDASE, HAO1) AND METHODS OF USE THEREOF
Last updated:
Abstract:
The invention relates to polynucleotide agents targeting an hydroxyacid oxidase (HAO1) gene, and methods of using such polynucleotide agents to inhibit expression of HAO1 and to treat subjects having an HAO1-associated disease, e.g., hyperoxaluria.
Status:
Application
Type:
Utility
Filling date:
3 Feb 2021
Issue date:
30 Dec 2021